In September 2019, the Myeloproliferative Neoplasm (MPN) Research Foundation (MPNRF) held a public, externally-led Patient-Focused Drug Development meeting. The objective was to capture specific needs from patients with MPNs and provide them with a forum to describe the impact of their disease, its associated symptoms and the burden of their disease on daily life. Additionally, patients provided their insights regarding current and emerging treatment options. The resultant “The Voice of the Patient Report for Myeloproliferative Neoplasms” was published in October 2021, which captured these findings.
Subsequently, MPNRF hosted a two-day virtual roundtable with thought leaders in the field to further examine issues relevant to the MPN community, including disease detection and developing patient-centered clinical endpoints. This article highlights disease-specific background information, unmet needs identified in The Voice of the Patient Report, and key takeaways from portions of each day of the roundtable that may help to address unmet needs for patients with MPNs.